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About Duchenne
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Clinical Trials
A quick look at investigational drug studies
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Female Carriers
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Team Jett
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Resource Library
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Resources for Partners
How To Help
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Clinical Trials
A quick look at investigational drug studies.
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Duchenne News
Stay up to date with the latest discoveries.
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Dan and DMD & Other Books
These books will help parents, guardians, and individuals as they navigate a Duchenne diagnosis and journey.
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Our Insurance Flight Plan
Our Health Insurance Flight Plan breaks down options that may be available to you.
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Resource Library
Read about our resources for Medical Professionals.
Resources for Medical Professionals
Join Jett Foundation’s Community Webinar Series to hear from the team at Wave Life Sciences on an overview of initial clinical trial results for WVE-N531 in individuals with Duchenne muscular dystrophy who are amenable to exon 53 skipping, as well as an overview of the potentially registrational FORWARD-53 study.
Wave Life Sciences: WVE-N531
Thursday, December 5, 2024
10am ET | 9am CT | 8am MT | 7am PT
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Anne-Marie Li-Kwai-Cheung joined Wave in February 2022 as Senior Vice President, Regulatory Affairs, Compliance and Policy and was promoted to Chief Development Officer in September 2022. In her current role, Anne-Marie oversees all preclinical and clinical drug development activities at Wave.
Anne-Marie was previously at Roche (Basel, Switzerland), where she started in Global Regulatory Affairs and went on to hold leadership positions of increasing responsibility in global drug development and global program leadership within the neurology and rare disease therapeutic areas. She served as Life Cycle Leader for tominersen in Huntington’s disease, guiding the Phase 3 program and other late-stage development activities, including responsibility for commercial activity, reimbursement, medical affairs, development and manufacturing and supply. In addition, she led the filing and development team at Roche through the global launch of Ocrevus for multiple sclerosis. Her career also reflects her keen interest in personalized medicines, as she led a team focused on the development of novel digital outcome measures for neurological diseases, and software as a medical device (SaMD) to enable physicians and patients to better understand and manage disease progression. Prior to her work at Roche, Anne-Marie worked for Genzyme, leading regulatory teams in regulatory filings and a filing team for an advanced therapy during a period of significant legislative changes. With more than 20 years’ experience across major pharmaceutical companies, including GlaxoSmithKline and Wyeth, Anne-Marie has broad experience with the execution of strategic development and regulatory plans that deliver timely and meaningful therapies for patients.
Our Community Webinar Series is focused on ensuring that our Duchenne and rare disease community is better prepared for those unexpected moments, challenging medical decisions, and difficult stages when on a Duchenne journey.
No one ever expects Duchenne and there is no correct way to tackle a diagnosis, but we can always better prepare. This webinar series is an opportunity to equip yourself with more knowledge, resources, and tools for those real-life, often unanticipated, scenarios.
Tune in on February 29 to hear from our panel and moderators on how they are accomplishing goals and living life to the fullest!
Your gift helps Jett Foundation provide programming and opportunities, such as Camp Promise, to many families impacted by Duchenne muscular dystrophy each year.