Duchenne News

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June 27, 2022
On Saturday, June 25, 2022, Italfarmaco Group shared a press release regarding positive topline data from its completed Phase 3 EPIDYS trial with Givinostat.
June 23, 2022
On June 23, 2022, Sarepta shared news regarding the MOMENTUM study.
Pliant Therapeutics
June 23, 2022
On June 22, 2022, Pliant Therapeutics announced the presentation of pre-clinical data from one of its developing drug candidates, PLN-101325.
Edgewise Duchenne News
June 21, 2022
On June 20, 2022, Edgewise Therapeutics announced positive results from the ARCH open label study of EDG-5506.
PTC Duchenne News
June 20, 2022
On June 20, 2022, PTC Therapeutics, Inc. announced they will be hosting a call to review topline results from Study 041 for Translarna.
Sarepta
June 9, 2022
On June 9, 2022, Sarepta provided a community update on their actively recruiting clinical trial programs for Duchenne muscular dystrophy.
NS Pharma
June 2, 2022
On May 31, 2022, NS Pharma shared a press release on the 2-y interim analysis from the study of viltolarsen.
May 13, 2022
On May 11, 2022, Entrada Therapeutics shared a news release that included a presentation on new data supporting its growing pipeline of EndosEscape Vehicle (EEVTM) Therapeutics at TIDES USA 2022.
May 5, 2022
On May 4, 2022, REGENXBIO issued a press release ahead of its First Quarter 2022 financial results. The release announces a delay in dosing of the first patient in the Phase I/II AFFINITY DUCHENNE trial, to first half 2023.
April 27, 2022
Solid Biosciences shared a press release with an organizational update to advance the development of their Duchenne Gene Therapy Pipeline Programs.