Community Webinar: The Vamorolone Summit Study
Join us for an informative webinar with Dr Nadeem Khaliq of Catalyst and Dr Kaitlin Batley of Children’s Health Specialty Center, Dallas.
Community Webinar: Pressure Ulcer Prevention and Treatment
Tune in to hear from Dr. David German and Danielle Dwiggins, RN, BSN and mom to a son living with Duchenne, who will speak on pressure ulcer prevention and treatment.
Community Webinar: Topline Data from EXPLORE44® Clinical Trial
Tune in on the first of May to hear from the team at Avidity Biosciences on topline data from their EXPLORE44® clinical trial, which is assessing the safety and efficacy of the investigational therapy delpacibart zotadirsen (formerly AOC 1044, abbreviated as del-zota) in people living with Duchenne muscular dystrophy mutations amenable to exon 44 skipping […]
Community Webinar: Opportunities for Financial Autonomy & Independence Through ABLE Accounts
Tune into a discussion around ABLE (Achieving a Better Life Experience) accounts and how they can help families managing the financial challenges of Duchenne muscular dystrophy.
Clinical Impact of FORCETM Platform in Duchenne
Please join us during our Community Webinar Series on April 17th as we welcome the team from Dyne Therapeutics to speak on updates to the DELIVER trial of DYNE-251 in males with Duchenne mutations amenable to exon 51 skipping. Clinical Impact of FORCETM Platform in Duchenne April 17, 2025 | 1pm ET| Zoom
Community Webinar: Targeting Bone Health in Duchenne (SHIELD DMD)
Jett Foundation’s Community Webinar Series with a presentation from Dr. Maitea Guridi on Roche’s SHIELD DMD and targeting bone health in Duchenne muscular dystrophy.
Community Webinar: Navigating Your Emotional Journey Following Genetic Diagnosis
Jett Foundation’s Community Webinar Series featuring Mary-Frances Garber, who will present on navigating your emotional journey following a genetic diagnosis, such as Duchenne muscular dystrophy.
Community Webinar: REGENXBIO AFFINITY DUCHENNE Pivotal Trial and Interim Functional Data
Tune in to Jett Foundation’s Community Webinar Series to hear from the team at REGENXBIO on their RGX-202 AFFINITY DUCHENNE Pivotal Trial and Interim Functional Data.
Community Webinar: NS Pharma Exon Skipping Trials Brogidirsen and NS-050/NCNP-03
NS Pharma will present information on two enrolling exon skipping clinical studies: a Phase II study evaluating Brogidirsen (exon 44) and a Phase I/II study evaluating NS-050/NCNP-03 (exon 50).
Community Webinar: Wave Life Sciences Interim Results from FORWARD-53 Study of WVE-N531
Wave will provide an overview of initial clinical trial results for WVE-N531 in individuals with Duchenne muscular dystrophy who are amenable to exon 53 skipping, as well as an overview of the potentially registrational FORWARD-53 study.
Community Webinar: Cardiac Devices
Tune in to hear from Andreas Barth on cardiac devices in Duchenne, Becker, and Carrier patients with an emphasis on implanted devices.
Community Webinar: Practical Applications of 3D Printing
Bruce Ward and Matt Bollinger share their experiences using 3D printing in everyday life.
Community Webinar: Solid Biosciences’ INSPIRE DUCHENNE Update and Study Expansion
Solid will provide an update on INSPIRE DUCHENNE, clinical trial for SGT-003, a next-generation microdystrophin gene therapy for individuals living with Duchenne muscular dystrophy.
