Thriving With Duchenne Episode with Two Disabled Dudes Podcast
A Rare Disease Day podcast recording from the Two Disabled Dudes, Kyle Bryant and Sean Baumstark, who moderated Jett Foundation’s 2024 Rare Disease Day event.
Overjoyed About Accessibility
Overjoyed is a new way to create and play digitally turning small mouse movements into key presses and other actions, allowing even people with low to no dexterity or movement to control their computer.
PPMD’s Gene Therapy Hub
Gene therapy has made significant strides in Duchenne muscular dystrophy, with one therapy approved and other potential therapies in various stages of development. PPMD’s resources aim to empower and inform families like yours, providing insights and guidance to help you better understand the dynamic landscape of gene therapy.
Six Core Elements of HealthCare Transition: Integrating Young Adults into Adult Health Care
Got Transition dives deep into how to best transition young adults into adult health care.
Six Core Elements of HealthCare Transition: Transitioning to an Adult Approach to Health Care Without Changing Clinicians
Curious about transition of health care when clinicians aren’t being changed? Got Transition provides a package and explanations for the best approach.
Health Care Transition Quiz for Youth and Young Adults
Are you ready to transition to adult health care? Take this Got Transition quiz for help on what works best for you and your timeline.
ASGCT Gene Therapy 101
This Gene Therapy Basics webpage from the American Society of Gene + Cell Therapy helps with understanding genes through descriptions, visuals, and videos.
State-Specific Resources by PPMD
Helpful topics and Duchenne help, categorized by each of the 50 U.S. States.
Little Hercules Foundation Resources
Links and support for families impacted by Duchenne from financial services to travel to clinical trials.
Physical Therapy for Families & Caregivers by CureDuchenne
A guide and benefits to physical and occupational therapy for families impacted by Duchenne.
State-Specific Resource Guide
A dynamic list of resources and tools for the Duchenne community, broken down by state.
PPMD: Duchenne 101
An overview of Duchenne, its genetic causes, progression, types of mutations, and more.
MDA Care Center Network
Click to visit a list of Muscular Dystrophy Association’s care center locations in the United States. The MDA Care Center Network offers tens of thousands of appointments each year for individuals living with muscular dystrophy, ALS, and other neuromuscular diseases to access expert multidisciplinary care, clinical trials, and to connect with MDA and the neuromuscular community.
