PPMD’s Gene Therapy Hub

Gene therapy has made significant strides in Duchenne muscular dystrophy, with one therapy approved and other potential therapies in various stages of development. PPMD’s resources aim to empower and inform families like yours, providing insights and guidance to help you better understand the dynamic landscape of gene therapy.

CureDuchenne’s DME Guide

This Durable Medical Equipment (DME)Guide has been developed by CureDuchenne to provide families and caregivers with a comprehensive resource of beneficial equipment.

ASGCT Gene Therapy 101

This Gene Therapy Basics webpage from the American Society of Gene + Cell Therapy helps with understanding genes through descriptions, visuals, and videos.